News from November 2025

The Access to Medicines and Medical Devices APPG has written to the Health Minister to highlight ongoing challenges with the Early Access Programme (EAP) for Givinostat, a life-changing treatment for Duchenne muscular dystrophy.

The Access to Medicines and Medical Devices APPG has written to the Health Minister to raise concerns about ongoing delays in the UK National Screening Committee’s review of newborn screening for Spinal Muscular Atrophy (SMA).